Monoclonal antibody treatment for protein misfolding diseases
Target misfolded proteins in ALS and Alzheimer's; Develop therapies for AL, ATTR, and ALECT2 amyloidosis; Conduct FDA clinical trials for lead candidates; Provide hope for patients with rare diseases; Combat multi-organ failure caused by protein misfolding
Three pre-clinical stage antibodies with commercial interest; Team includes experts in monoclonal development and protein biochemistry; Addresses a global healthcare crisis affecting 300 people per million worldwide