Pharmaceutical company targeting nephrogenic diabetes insipidus
Treat children with nephrogenic diabetes insipidus; Address severe dehydration in NDI patients; Develop therapies for congenital NDI; Research genetic mutations affecting vasopressin receptors; Collaborate with strategic partners for drug development
Announced leadership appointments including Dr. Jeff Sands as Chief Medical Officer; Entered agreement with MSRD and Otsuka for NDI treatment development