Transformative genetic therapies for rare diseases
Location
Somerville, Massachusetts, United States
Employees
201-500
Founded
1992
Funding Category
Series A
Product Features & Capabilities
LYFGENIA
ZYNTEGLO
SKYSONA
Patient support services
Clinical trials monitoring
Other Considerations
Transitioned to a privately held company in 2025; Newly appointed leadership team with extensive biotech experience; Strong focus on commercial execution and patient access