Transformative genetic therapies for rare diseases
HQ Country
Somerville, United States
Employees
201-500
Founded
1992
HQ State/Province
Massachusetts
Funding Category
Series A
HQ Full Address
Somerville, Massachusetts, United States
Product Features & Capabilities
LYFGENIA
ZYNTEGLO
SKYSONA
Patient support services
Clinical trials monitoring
Other Considerations
Transitioned to a privately held company in 2025; Newly appointed leadership team with extensive biotech experience; Strong focus on commercial execution and patient access