Target microRNAs in heart failure; Treat dry age-related macular degeneration; Address aging-related sarcopenia; Manage Duchenne and Becker muscular dystrophies; Deliver ASOs to previously inaccessible tissues
Founded by Anders M. Näär, PhD, UC Berkeley Professor of Metabolic Biology; Based in Bakar Labs biotech incubator at UC Berkeley; Early-stage clinical data in non-human primates and pigs; Employee count of 2-10; Founded in 2021